International Neonatal Screening Day 👣
On this day we raised awareness of our efforts to get ALD added to the UK newborn screening programme on our social media channels. See our posts below:
Here are the latest news stories from Alex TLC and about topics we think you'll find useful.
On this day we raised awareness of our efforts to get ALD added to the UK newborn screening programme on our social media channels. See our posts below:
SwanBio Presents Design of Innovative Natural History Study Aimed to Evolve Understanding of Adrenomyeloneuropathy and Inform Future Treatments SwanBio have released a press release about their AMN natural history study using wearable technology – with the data collected to provide insights for future first-in-human study of SBT101, AAV-based gene therapy for AMN.
No further manufacturing of injectable Hydrocortisone Sodium Phosphate We have been informed that there will be no further manufacturing of injectable Hydrocortisone Sodium Phosphate by Advanz Pharma until 2023.
Should ALD be included as part of the newborn screening programme? Are you a man aged 16 and over affected by ALD/AMN? Or their family member/carer?
Gene Therapy for AMN Clinical Trial Update SwanBio Therapeutics have announced additional preclinical data that supports Clinical Advancement of First AAV-Based Gene Therapy for Adrenomyeloneuropathy. SBT101 preclinical studies demonstrate improvement in behavioral and biochemical markers of disease. Further support for dosing strategy for Phase 1/2 study initiating later in 2022.
Granted Orphan Drug US Designation Poxel Announces PXL065 and PXL770 Granted Orphan Drug Designation from the U.S. FDA for X-Linked Adrenoleukodystrophy.