Newborn Screening Article
By Sara Hunt, Our CEO
Our CEO, Sara’s, article ‘Why Teddi’s MLD gene therapy story should provoke immediate change for newborn screening’ has been featured in National Health Executive Magazine. Sara discusses the recent announcment that gene therapy is available for families of children affected with MLD. She highlights the vital need for newborn screening for MLD and ALD, and how early diagnosis could help ensure treatment is available for all affected children instead of those identified early, usually through sibling diagnosis.
To read her article, see page 50: NHE Magazine