Canavan Disease Trial Update
Positive Update to share with the Canavan Community Aspa Therapeutics have shared additional encouraging data from the CANaspire gene therapy trial.
Here are the latest news stories from Alex TLC and about topics we think you'll find useful.
Positive Update to share with the Canavan Community Aspa Therapeutics have shared additional encouraging data from the CANaspire gene therapy trial.
Presentations available to view ELA International Families and Research Meeting was held on 15th and 16th April. Recorded presentations from the event are now available to view on the ELA International website. Click here to access the videos: Families/Researchers Meeting Presentations
An interesting article in LiveScience The article discusses what gene therapy is, what it does to your DNA, how it works and whether it’s safe. To read: https://www.livescience.com/gene-therapy-everything-you-need-to-know-about-the-dna-tweaking-treatments
May 2023 Our Research Summary for May 2023 is ready to view.
Another ask from a community member We have another Ask Our Community for May. One of our community members is asking for some advice. Her adult son wants to write a book about his life with Adrenoleukodystrophy (ALD). He is unable to write the book himself and would need support when developing the content of the book.
Vanishing White Matter Disease Trial Update Calico has announced that ‘the first participant has been dosed in a Phase 1b clinical trial, (study M23-523; NCT05757141), evaluating the investigational eIF2B activator ABBV-CLS-7262 as a potential treatment for Vanishing White Matter (VWM) disease’.